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Since 1874 遺伝子治療とゲノム編集治療の 研究開 …

NIHSS ince 1874 NIHSS ince 1874 1 1 2 3 Invivo ex vivo ( ) T AAV DNA 7 4*J Gene data B ADA LPL HIV/AIDS B ALS 65%

NIHS Since 1874. NIHS. Since 1874. 遺伝子治療とゲノム編集治療の. 研究開発の現状と課題. 国立医薬品食品衛生研究所. 遺伝子医薬部

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